Aspen Neuroscience, Inc. yalengeza kuti mwezi uno ikhazikitsa kafukufuku woyamba wowunika odwala amtundu wake, akugwira ntchito ndi malo angapo owunika zachipatala ku US.
Gulu la Trial-Ready Cohort Study la kampaniyi ndi gawo loyamba lolemba fomu yofunsira Investigational New Drug (IND) ku US Food & Drug Administration ya ANPD001, yemwe ndi woyamba kulandira chithandizo chamankhwala omwe angathe kuchiza matenda a idiopathic Parkinson (PD). Kafukufuku wa Trial-Ready Cohort apereka chidziwitso ndikuwonetsa omwe angathe kukhala odwala pagawo la 1/2A lachipatala loyamba la odwala a ANPD001. Kampaniyo ilengeza malo angapo owonera aku US nthawi yonse yamasika.
"Iyi ndi nthawi yodziwika bwino kwa odwala komanso ku gulu la Aspen Neuroscience, pamene tikutsegula kafukufuku wathu woyamba kuti tifufuze kafukufuku wathu wokhudza chithandizo chamankhwala chochokera ku iPSC cha matenda a Parkinson," atero a Damien McDevitt, Ph.D., Purezidenti ndi wamkulu. mkulu wamkulu. "Ndife okondwa komanso odzichepetsa kuti tiyambe gawo lotsatira pa Mwezi Wodziwitsa a Parkinson. Ichi ndi sitepe yofunika kwambiri kwa anthu odwala, kwa opereka chithandizo chamankhwala ndi gawo la neuroscience. "
PD ndi matenda achiwiri odziwika bwino a neurodegenerative, omwe amakhudza pafupifupi anthu miliyoni aku America komanso anthu opitilira mamiliyoni khumi padziko lonse lapansi. Ngakhale ndi mulingo waposachedwa wa chithandizo chamankhwala, odwala amatha kukhala ndi zovuta zamagalimoto zofooketsa chifukwa cha kutayika kwa ma dopamine neurons muubongo; pafupifupi 50% amatayika ngakhale asanazindikire.
Aspen Neuroscience ndiye kampani yotsogola yomwe ikupanga choloweza m'malo mwamunthu chomwe chingathetse kufunikira kwa chithandizo cham'thupi. Njirayi imagwiritsa ntchito ma iPSC omwe amapangidwa ndi khungu la wodwala kuti apange ma dopamine neurons kuti abwezerenso wodwala yemweyo. Kupangidwa kuchokera ku khungu losavuta la biopsy, maselo a wodwala aliyense adzawunikidwa kuti agwire bwino ntchito pogwiritsa ntchito zida za genomics zochokera ku AI, asanawaike kuti agwiritsidwe ntchito kuchipatala.