Gawo limodzi kuyandikira chithandizo chatsopano cha Cystic Fibrosis

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Written by Linda Hohnholz

Entrinsic Bioscience ndi chilolezo chake Nuvara Therapeutics adalengeza kuti ali gawo limodzi loyandikira kugwiritsa ntchito ma RxAA monga chithandizo cha odwala omwe ali ndi masinthidwe a Cystic Fibrosis Class I. Wofufuza pa yunivesite ya Florida Dr. Sadasivan Vidyasagar, yemwe anayambitsa ndi tcheyamani wa bungwe la alangizi a sayansi la kampani, posachedwapa adagawana njira ina yobwezeretsa katulutsidwe ka anion a airway pamsonkhano wa Experimental Biology 2022 womwe unachitikira ku Philadelphia.      

Vidyasagar ndi gulu lake, kuphatikiza ofufuza a UF ndi Entrinsic Bioscience, adawonetsa kuti formula ya Nuvara ya VS-009 ikhoza kukhala yopindulitsa kwa odwala omwe ali ndi masinthidwe a Cystic Fibrosis Class I komanso masinthidwe a Class II ndi III. Mankhwalawa atha kugwiritsidwa ntchito okha kapena kuphatikiza ndi mankhwala ena kuti apititse patsogolo katulutsidwe ka kloride.

Stephen J. Gatto, Wapampando Wachiwiri wa Nuvara Therapeutics, adayamikira Astrid Grosche ndi gulu lonse la Dr. Vidyasagar chifukwa cha kudzipereka kwawo poyendetsa njira zatsopano zowunika ntchito ya kupuma kwa epithelial.

"Ndikufuna kuthokoza Astrid, Dr. Vidyasagar ndi gulu lake lonse chifukwa cha kudzipereka kwawo mwakhama kuti athetse kusintha kwa Class I mu Cystic Fibrosis, kusintha komwe kungakhudze 18% ya anthu a CF," adatero Stephen J. Gatto.

"Zing'onozing'ono ziwirizi zikuwonetsa kuti kusintha kwa ion-channel ndikotheka mu epithelium yopuma pogwiritsa ntchito ma amino acid," adatero Gatto. "Kusokonekera kwa ion-channel ndikofunikira pamatenda ambiri, monga CF ndi matenda omwe amachulukirachulukira, kuphatikiza mphumu ndi COPD. Njira / zochizira izi zidzatilola kuti tisinthe kuchuluka kwa ma ion ndi madzi mumsewu wam'mlengalenga pamlingo wa ma cell okhala ndi zotsatira zochepa.

"Pali ntchito yoti ichitike, koma mwayiwu ndi wosangalatsa kwambiri ndipo ukhoza kuyimira kupambana pa kayendetsedwe ka ma channelopathies ndi matenda okhudzana nawo," adatero Gatto.

Vidyasagar adaperekanso chithunzi pazida zomwe labu yake adapanga kuti azitha kuyeza bwino matumbo a peristalsis komanso kuphatikizika kwa kuthamanga kwa intraluminal, kupindika kwa minofu, komanso kusintha kwamadzimadzi.

"Zing'onozing'ono ziwirizi ndizopadera chifukwa zimasonyeza kuti zimatha kusintha mapuloteni a epithelial transmembrane (eTMPs) ndi mapangidwe osankhidwa a amino SAA (RxAAs)," adatero Dr. William Denman, Chief Medical Advisor ku Nuvara Therapeutics. "Izi zimatsegula chitseko cha chithandizo chamankhwala chogwira mtima, chosakhala ndi poizoni pamlingo woyambira ma cell, mosasamala kanthu za etiology."

Dr. Denman anapitiriza kunena kuti: “Machiritso a m’tsogolo tsopano akhoza kutsimikiziridwa ndi kulinganiza njira ndi matenda—mankhwala enieni odziŵika munthu payekha. Ntchito yochulukirapo ikufunika, koma izi zitha kulola njira zina zochiritsira pamlingo wa ma cellular pamitundu yonse ya matenda omwe alibe zotsatirapo zochepa. ”

Entrinsic Bioscience ndiwoyambitsa UF womwe uli ku UF Innovate | Fulumirani ku Sid Martin Biotech ku Alachua. Kampaniyo ikupanga mitundu yonse yachilengedwe, yopanda shuga ya hydration, thanzi lamatumbo ndi thanzi, ziwengo, ndi chisamaliro cha khungu.

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Linda Hohnholz

Mkonzi wamkulu kwa eTurboNews zochokera ku eTN HQ.

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